Gene correction of CD40LG gene in T cells and HSPC for the treatment of X-linked hyper-IgM immunodeficiency
- 5 Anni 2016/2021
- 491.603€ Totale Fondi
Descrizione non disponibile
Pubblicazioni Scientifiche
- 2017 SCIENCE TRANSLATIONAL MEDICINE
Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1
