Patients' stories

01 / 02

Tommaso was treated for ADA-SCID in February 2016 at the San Raffaele Telethon Institute in Milan (SR – Tiget).

News from Research

02 / 02

Gene therapy, especially if administered early, could be an effective treatment strategy for beta thalassemia, a genetic disease that is quite common in Mediterranean countries, affecting over 7000 patients in Italy only.

This investment brings the total financing by Sofinnova Partners to €25 million over the past six months.

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