The 30 members of the Telethon Scientific Committee on June 20-21 gave their final assessment of 160 projects that have passed...
- Announced the submission of a marketing application
- to the European Medicines Agency (EMA) for a gene therapy.
- Read more.
Based on research carried out at the San Raffaele Telethon Institute for Gene Therapy (TIGET) in Milan, a technique has been developed that allows bad genes to be repaired directly on the DNA strand of human blood stem cells. The study, published in the scientific journal Nature, will make gene therapy more precise. Read more
Willing to donate?
or input the desired amount
Seleziona la tua regione
Did you know?
The first case of successful gene therapy in the world was achieved by TelethonDid you know?
2532 projects on 449 genetic disorders, with a direct investment of more than € 423 millionsRead more