The 30 members of the Telethon Scientific Committee on June 20-21 gave their final assessment of 160 projects that have passed...
- Announced the submission of a marketing application
- to the European Medicines Agency (EMA) for a gene therapy.
- Read more.
New hope of a cure for genetic mitochondrial diseases, which in children can cause slowing or stopping of growth, progressive encephalopathy, severe muscle disorders, cardiomyopathies.
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The first case of successful gene therapy in the world was achieved by TelethonDid you know?
2532 projects on 449 genetic disorders, with a direct investment of more than € 423 millionsRead more