• Announced the submission of a marketing application
  • to the European Medicines Agency (EMA) for a gene therapy.
  • Read more.

Latest news


The 30 members of the Telethon Scientific Committee on June 20-21 gave their final assessment of 160 projects that have passed...


Based on research carried out at the San Raffaele Telethon Institute for Gene Therapy (TIGET) in Milan, a technique has been developed that allows bad genes to be repaired directly on the DNA strand of human blood stem cells. The study, published in the scientific journal Nature, will make gene therapy more precise. Read more