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From epigenetics - new molecular switches to silence genes

From epigenetics - new molecular switches to silence genes

A new gene silencing strategy has been developed at the San Raffaele-Telethon Institute for Gene Therapy (SR-Tiget) that allows permanent silencing of genes by acting on epigenetic processes that regulate their reading and translation into proteins.

Editas Medicine Announces Scientific Multi-Year Collaboration with Fondazione Telethon and Ospedale San Raffaele

Editas Medicine Announces Scientific Multi-Year Collaboration with Fondazione Telethon and Ospedale San Raffaele

Company to Collaborate with Leading Genomic Medicines Institutes to Progress Genome Edited Hematopoietic Stem Cell and T Cell Based Therapies

Preliminary results reporting the safety and effectiveness of gene therapy in patients with metachromatic leukodystrophy published in The Lancet

Preliminary results reporting the safety and effectiveness of gene therapy in patients with metachromatic leukodystrophy published in The Lancet

A gene therapy with vectors derived from HIV virus has been developed in the laboratories of the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget) in Milan. Preliminary results reporting the safety and efficacy of this investigational gene therapy for early treatment of the early onset forms of a rare genetic disease, metachromatic leukodystrophy have been published in The Lancet.

Strimvelis receives European marketing authorisation to treat very rare disease, ADA-SCID

Strimvelis receives European marketing authorisation to treat very rare disease, ADA-SCID

GSK, Fondazione Telethon and Ospedale San Raffaele gain approval to provide life-saving gene therapy to patients