We consider research the only way forward to finding treatments for genetic diseases
In order to actively and proactively further Italy’s culture of science, we constantly engage in dissemination, information and awareness-raising activities. Our aim is to optimize Italy’s research system. We wish to remove all factors hampering our researchers as they seek to provide concrete answers to people who must struggle against genetic diseases. All this is part and parcel of our mission. This is precisely why we have formulated clear, transparent, future-oriented positions with regard to certain issues.
Fondazione Telethon pursues cooperation strategies to merge competencies with private companies in order to achieve full therapeutic development of the results obtained by its research.Learn more
Our mission consists in funding the kind of research that may provide treatments for genetic diseases. We also oppose mistreatment of animals.LEARN MORE
Strimvelis: Telethon experience
Strimvelis, the first ex-vivo gene therapy intended to treat patients with a ADA-‐SCID, is the epitome of a product born thanks to a strategic alliance between a non-profit organization and a pharma company.Learn more
Accelerating ATMP development
The development of advanced therapies is among the main challenges of biomedicine, not only in the field of rare diseases. In this document, the scientists of the San Raffaele-Telethon Institute for Gene Therapy (SR-Tiget), whose mission consists in performing cutting edge research on gene and cell therapy and translating its results into therapeutic advances for genetic diseases, suggest tre topics to provide a substancial advances in this field.Learn more