Research, partnership, merit, excellence. All our official positions.

We consider research the only way forward to finding treatments for genetic diseases

In order to actively and proactively further Italy’s culture of science, we constantly engage in dissemination, information and awareness-raising activities. Our aim is to optimize Italy’s research system. We wish to remove all factors hampering our researchers as they seek to provide concrete answers to people who must struggle against genetic diseases. All this is part and parcel of our mission. This is precisely why we have formulated clear, transparent, future-oriented positions with regard to certain issues.

Our alliances

Fondazione Telethon pursues cooperation strategies to merge competencies with private companies in order to achieve full therapeutic development of the results obtained by its research.

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Animal trials

Our mission consists in funding the kind of research that may provide treatments for genetic diseases. We also oppose mistreatment of animals.


Strimvelis: Telethon experience

Strimvelis, the first ex-­vivo gene therapy intended to treat patients with a ADA-­‐SCID, is the epitome of a product born thanks to a strategic alliance between a non-­profit organization and a pharma company.

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Responsible Conduct of Research (RCR) and Research Integrity (RI)

Fondazione Telethon works to preserve and promote the responsible conduct of research (RCR) within the Telethon-funded research community. Research integrity (RI) is the basis of RCR and standard principles of RI are shared within the international scientific community, as laid out by the European Code of Conduct for Research Integrity.

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Accelerating ATMP development

The development of advanced therapies is among the main challenges of biomedicine, not only in the field of rare diseases. In this document, the scientists of the San Raffaele-Telethon Institute for Gene Therapy (SR-Tiget), whose mission consists in performing cutting edge research on gene and cell therapy and translating its results into therapeutic advances for genetic diseases, suggest tre topics to provide a substancial advances in this field.

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